Gene mutation that ‘reduces odds of Alzheimer’s disease by 70%’ discovered

A gene mutation that reduces the odds of developing Alzheimer’s disease by 70% has been discovered by scientists. This “protective” variant occurs in a gene – FN1 – which makes a protein ... Read More

AscellaHealth Unveils Quarter’s Insights on Specialty and Rare Disease Drug Developments

This quarterly digital publication stands as the industry’s most detailed resource on imminent specialty and rare disease drug launches, including cell and gene therapies (CGT), biosimilars ... Read More

A lifesaving therapy for children with a rare disease is now the world’s most expensive drug, raising questions about access

Lenmeldy was approved by the US Food and Drug Administration on Monday and is the first therapy for the rare and devastating disease ... that as the list of gene and cell therapies with eye ... Read More

An opening for an ultra-rare disease drug

That’s a longstanding issue with rare-disease drug ... at increased risk for the disease, the company said Tuesday, a move that would make the shot the first of its kind. A late-stage clinical ... Read More

Woman's 'one-of-a-kind' disease causes thousands of TUMORS to grow all over her body- including in her nose and mouth

A woman with a rare disease ... s disease and it occurs because of a mutation on a person's NF-1 gene. This gene regulates a protein that plays a role in cell growth and is thought to be ... Read More

New bill could require insurance to cover medication for rare autoimmune disease

Families of children with a rare autoimmune disorder are ... Doctors say her therapies are working and, for now, the disease in remission. San Jose native Len Ramirez has been a news reporter ... Read More

Opinion: The revolutionary sickle cell therapies

Having two innovative therapies to treat a disease ... in contrast to germ cell gene editing, which is banned.” The US Department of Health and Human Services recently announced that it ... Read More

Progress Announces First Quarter 2024 Financial Results

March 26, 2024 (GLOBE NEWSWIRE) -- Progress (Nasdaq: PRGS), the trusted provider of infrastructure software, today announced financial results for its fiscal first quarter ended February 29 ... Read More

Existing medicine may slow rare disease that can lead to amputation

There's a glimmer of hope for people afflicted by a rare ... Alzheimer's disease -- suggesting the drugs might also lower risks for the brain illness. Health News // 1 day ago White House ... Read More

Lululemon releases a first-of-its-kind product

In February, Lululemon announced the arrival of a new material ... And on Wednesday, Lululemon dropped its first-ever product made with enzymatically recycled polyester, made in partnership ... Read More

How often total solar eclipses happen — and why Monday's was so rare

On April 8, a rare total solar eclipse drew a "path of totality" over North America, throwing swaths of the United States, Canada and Mexico into darkness in the middle of the day. A solar eclipse ... Read More

Meta announces a Quest product to help teachers engage students 13 and up

The company announced a new education-focused product on Monday, one that lets teachers, trainers, and administrators control what apps are on connected headsets and lets them manage multiple ... Read More